Certified Pediatric Hematology Oncology Nurse (CPHON) 2025 – 400 Free Practice Questions to Pass the Exam

Beta Thalassemia is a genetic blood disorder characterized by reduced production of hemoglobin, which can lead to anemia and other complications. A common treatment option for managing severe cases of Beta Thalassemia is bone marrow transplantation. This procedure can be curative for patients, particularly when performed early in life. Bone marrow transplantation involves replacing the patient's defective bone marrow with healthy stem cells from a compatible donor, which can help restore normal hemoglobin production.

While stem cell therapy is somewhat related and can involve the use of bone marrow, the specific reference to bone marrow transplantation emphasizes a well-established treatment option, especially for severe cases where a suitable donor is available. This approach aims to provide a long-term resolution to the underlying cause of the disease.

Other treatment modalities, while important in managing symptoms or specific complications of Beta Thalassemia, are not considered curative. For instance, radiation therapy is generally not applicable as a treatment for Beta Thalassemia, and chemotherapy is primarily employed in the context of malignancies rather than this hematologic disorder. Therefore, bone marrow transplantation stands out as the most definitive treatment for individuals suffering from significant forms of Beta Thalassemia.